---
title: "Sanofi Pompe drug shortages, Jazz Pharma buys Actio, and Lilly’s Foundayo OKed in U.K."
id: "stat-news-4-stat-pharmalittle-we-re-reading-about-a-sanofi-drug-shortage-a-jazz-pharma-deal"
canonical_url: "https://medichelpline.com/clinical-feed/stat-news-4-stat-pharmalittle-we-re-reading-about-a-sanofi-drug-shortage-a-jazz-pharma-deal"
content_type: "clinical_feed_article"
specialty: "Pharmacology"
source_name: "STAT News"
source_url: "https://www.statnews.com/pharmalot/2026/08/10/sanofi-drug-shortage-jazz-pharma-deal/?utm_campaign=rss"
published_at: "2026-08-10T13:24:23.000Z"
evidence_level: "Verified Feed"
license: "CC-BY-NC-4.0 / Informational Use"
---
# Sanofi Pompe drug shortages, Jazz Pharma buys Actio, and Lilly’s Foundayo OKed in U.K.
## Provenance & Clinical Metadata
- **Canonical URL:** https://medichelpline.com/clinical-feed/stat-news-4-stat-pharmalittle-we-re-reading-about-a-sanofi-drug-shortage-a-jazz-pharma-deal
- **Specialty:** [Pharmacology](https://medichelpline.com/clinical-feed/pharmacology.md)
- **Primary Source:** STAT News
- **Source URL:** [Original Journal Publication](https://www.statnews.com/pharmalot/2026/08/10/sanofi-drug-shortage-jazz-pharma-deal/?utm_campaign=rss)
- **Published At:** 2026-08-10T13:24:23.000Z
- **Evidence Rating:** Verified Feed
## Executive GIST (TL;DR)
- Sanofi has notified patient groups and physicians in the U.S. and Europe of dwindling supplies of two treatments for **Pompe disease**, citing a bottleneck in the final manufacturing stage and quality control problems at its Waterford, Ireland facility. The shortages involved older standard therapy **Myozyme** and the newer product **Nexviazyme**. The supply issues surfaced after the **U.S. Food and Drug Administration (FDA)** issued a warning about manufacturing problems at the Irish plant. - **Jazz Pharmaceuticals** agreed to acquire **Actio Biosciences** in a transaction valued at up to $1.32 billion to obtain an experimental therapy for **KCNT1-related epilepsy**, a rare inherited epilepsy with frequent seizures and developmental delays in children. The candidate, **ABS-1230**, showed seizure reduction in an early pediatric study and is being evaluated in a trial intended to support a U.S. approval filing. Actio estimates the U.S. patient population at about 2,500. - The **U.K. drug regulator** has authorized Lilly’s **Foundayo** for weight management and treatment of **type 2 diabetes**, according to the article header. (No further details about the authorization were reported in the source.) - The reporting is drawn from STAT’s Pharmalittle column by Ed Silverman (Aug. 10, 2026) with additional sourcing from Reuters and referenced STAT coverage. Remaining story details beyond the items above were behind a STAT+ paywall and not reported in the source provided.
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Test your knowledge with our new weekday mini crossword [ Start solving ](https://www.statnews.com/stat-mini-crossword/) [STAT Plus](https://www.statnews.com/stat-plus/)Newsletter[Pharmalot](https://www.statnews.com/category/pharma/pharmalot/) # Pharmalittle: We’re reading about a Sanofi drug shortage, a Jazz Pharma deal, and more ## U.K. ​drug regulator authorizes Lilly’s Foundayo for weight ​management and type ​2 diabetes * [Manage alerts for this article](https://www.statnews.com/my-account/edit/#emails) * Email this article * [Share this article](https://www.statnews.com/pharmalot/2026/08/10/sanofi-drug-shortage-jazz-pharma-deal/?utm_campaign=rss) ![an anthropomorphized red and blue pill illustrated in the style of the famous american gothic painting](https://www.statnews.com/wp-content/uploads/2015/11/PHARMALOT_LITTLE-copy-645x645.jpg) Alex Hogan/STAT ![](https://www.statnews.com/wp-content/uploads/2021/02/ed-s-avatar-small4-80x80.png) By [Ed Silverman](https://www.statnews.com/staff/ed-silverman/) Aug. 10, 2026 Pharmalot Columnist, Senior Writer ![](https://www.statnews.com/wp-content/uploads/2021/02/ed-s-avatar-small4-80x80.png) [Ed Silverman](https://www.statnews.com/staff/ed-silverman/) 1. [](https://www.linkedin.com/in/edsilverman/ "Linkedin") 2. [](https://x.com/Pharmalot "X") ed.silverman@statnews.com Ed’s stories explore prescription drug pricing, affordability and access, as well issues surrounding patents, litigation, and legislation. He is also the author of the morning [Pharmalittle newsletter](https://www.statnews.com/signup/pharmalittle/) and the afternoon [Pharmalot newsletter](https://www.statnews.com/signup/pharmalot/). Good morning, everyone, and welcome to another working week. We hope the weekend respite was relaxing and invigorating because that oh-too-familiar routine of meetings, deadlines, and the like has returned with a vengeance. You knew this would happen, yes? To cope, we are relying, as always, on a cuppa stimulation. Our choice today is honeybush vanilla turmeric. Feel free to join us. Remember, no prescription is required. Meanwhile, here are some tidbits to help you along. Best of luck accomplishing your goals today and, of course, do keep in touch. … **Sanofi is experiencing shortages of two medicines used to treat Pompe disease, and the problem emerged shortly after the U.S. Food and Drug Administration warned the company over manufacturing issues at the Irish facility where the drugs are made** , [STAT](https://www.statnews.com/pharmalot/2026/08/09/sanofi-pompe-disease-drug-shortage-myozyme-nexviazyme/) reports. In recent days, the drugmaker has alerted patient groups and physicians in both the U.S. and Europe that supplies of Myozyme, an older standard of care, and Nexviazyme, a newer treatment, are dwindling due to what has been described as a bottleneck in the final manufacturing phase, as well as quality control issues at its Waterford plant. Advertisement **Jazz Pharmaceuticals agreed to buy Actio Biosciences in a deal valued at ​up to $1.32 billion, adding an experimental treatment for ‌a rare inherited form of epilepsy that has no approved therapies** , [Reuters](https://www.reuters.com/legal/litigation/jazz-bets-epilepsy-treatment-with-up-132-billion-deal-actio-2026-08-10/) notes. The treatment, called ABS-1230, is being developed for KCNT1-related epilepsy, ​a severe disease that causes frequent seizures ​and developmental problems in children. KCNT1-related epilepsy affects about ​2,500 patients in the U.S., according to the company. ABS-1230 reduced seizures in ‌an ⁠early study of children and is being evaluated in a study intended to support a U.S. approval application. STAT+ Exclusive Story Already have an account? 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